Rare Diseases

Rare Disease development poses unique challenges and opportunities. Our experts develop insightful and innovative strategies to bring these ‘game changing’ products to patients within all therapeutic indications with a particular focus on the unmet needs within rare and orphan diseases.

Therapeutic Experience

Therapeutic Experience

In-depth Expertise

At tranScrip, we are helping our biotech and pharma clients realise the potential of their assets. tranScrip is helping shift the paradigm of therapeutic intervention and steer strategies to maximise efficient, expeditious and safe development.

We provide strategic expertise, therapeutic experience and operational excellence across the entire product lifecycle.

Case Study

Regulatory Success for a US-Based Gene Therapy Company in the EU

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Brochure

Rare Diseases Project Examples

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Contact Us

Our experienced physicians and scientists, together with our regulatory, clinical and commercial experts can support you to maximise the value of your products. Whatever your project requires, we have the expertise to meet your needs.